Gene therapy shows promise in ARC syndrome, a deadly childhood liver… | HappeningNow.news

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Gene therapy shows promise in ARC syndrome, a deadly childhood liver disease

Source Summary Published June 19, 2026 Brief Under 1 min brief
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Views 49 Community interest
Brief read Under 1 min brief 31 words

Summary

A new gene therapy has been used to successfully treat a deadly childhood liver disease in mice that model the disease, according to researchers at UCL and Great Ormond Street Hospital.

Read original at Medical Xpress

Coverage Context

Part of ARC coverage 39 tracked stories

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