After 30 Years, FDA Approves First-Ever Drug For a Rare Neurological… | HappeningNow.news

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After 30 Years, FDA Approves First-Ever Drug For a Rare Neurological Disorder

Alexander disease is a rare genetic neurological disorder that affects less than one in a million people worldwide. It leads to a multitude of problems, including a loss of mobility, seizures, and issues with speech, and it's often fatal.

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Alexander disease is a rare genetic neurological disorder that affects less than one in a million people worldwide. It leads to a multitude of problems, including a loss of mobility, seizures, and issues with speech, and it's often fatal. The disease is caused by a fault in the gene that makes glial fibrillary acidic protein (GFAP).

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