Science · 6 views
After 30 Years, FDA Approves First-Ever Drug For a Rare Neurological Disorder
Alexander disease is a rare genetic neurological disorder that affects less than one in a million people worldwide. It leads to a multitude of problems, including a loss of mobility, seizures, and issues with speech, and it's often fatal.
Summary
Alexander disease is a rare genetic neurological disorder that affects less than one in a million people worldwide. It leads to a multitude of problems, including a loss of mobility, seizures, and issues with speech, and it's often fatal. The disease is caused by a fault in the gene that makes glial fibrillary acidic protein (GFAP).
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